article · Hämostaseologie

Efficacy, safety, and quality of life 5 years after valoctocogene roxaparvovec gene transfer

A Leavitt
Jody M. Mason
K-M Chavele
Gillian Lowe
Dominic Pepperell
F. Peyvandi
Robert Klamroth
Carolyn M. Millar
Johnny Mahlangu
DV Quon
Emily Symington
G Kenet
S Pipe
N Key
H Chambost
P Raheja
E Majerus
A Giermasz
S-C Chou
M C Ozelo

2026University of the Witwatersrand

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Research topics

Virus-based gene therapy research
Complement system in diseases
Animal Genetics and Reproduction

Sustainable Development Goals

2Zero Hunger

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DOI: 10.1055/s-0045-1814584

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